Gene Therapy
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New Gene Therapy Uses Harmless Virus To Target Muscle Spasms, Study Finds
The findings showed that animals receiving the treatment experienced a gradual reduction in muscle spasticity. Significant improvements began to appear several weeks after therapy and continued over time.
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Scientists Develop Targeted Drug Delivery For Arresting Tumour Growth, Reducing Off-target Effects
Experiments in breast cancer models demonstrated a robust gene knockdown, resulting in an increased cancer cell death and a substantial inhibition in tumour growth.
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Biotech Firm MedTherapy Says It Can Cut Gene Therapy Production Time To One Day
A key claim by the company MedTherapy is a major reduction in production timelines. While gene therapies typically take weeks or months to manufacture, MedTherapy says it has significantly shortened the process.
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New One-Shot Gene Editing Therapy May Reduce Bad Cholesterol By 62%
A groundbreaking gene-editing therapy developed by Eli Lilly and Verve Therapeutics reduced "bad" LDL cholesterol by up to 62% after a single infusion in an early trial, raising hopes for a long-lasting treatment to reduce heart attack risk
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A New Gene Therapy May Restore Hearing In Weeks, Give People Born Deaf A Chance To Hear Again
The treatment targets a specific type of inherited deafness caused by mutations in a gene called OTOF.
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India's BioE3 Policy Is Advancing GeneEditing And Cell Therapy: Minister
The first-in-human Phase-I clinical trial for gene therapy of Hemophilia A has shown clinically significant outcomes.
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India Launches 1st Indigenous, Low-Cost Gene Therapy For Sickle Cell Disease
The world-class, low-cost gene editing solution named "BIRSA 101", in honour of Bhagwan Birsa Munda, remembered as a great tribal freedom fighter.
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Scientists Restore Ancient Gene To Help Treat Gout And Uric Acid Disorders
Scientists at Georgia State University have revived a 20-million-year-old gene called uricase, which may offer new hope in treating gout and related uric acid disorders by helping the body break down excess uric acid naturally.
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Indian-Made Gene Therapy For Blood Cancer Shows 73% Response Rate In Clinical Trials
An indigenously developed gene therapy for specific blood cancers has shown a 73 per cent response rate among patients in India, according to results of clinical trials published in The Lancet Haematology journal.
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GST Council Exempts Gene Therapy, Cuts Tax Rate For Rice Kernels
Jaisalmer (Rajasthan): Union Finance Minister Nirmala Sitharaman on Saturday announced that the Goods and Services Tax Council has approved the reduction of GST on rice kernels to 5 per cent and exempted life-saving gene therapy from tax.
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AI Unlocks “DNA Grammar” for Targeted Gene Editing, Enhancing Gene Therapy, and More
Researchers at The Jackson Laboratory, Broad Institute, and Yale University use AI to identify DNA sequences that control gene activation in specific cells. This AI model decodes patterns in DNA regions called cis-regulatory elements (CREs), guiding synthetic DNA switches for cell-specific gene activity. Early testing in animal models showed succes...
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1-Year-Old UK Girl's Hearing Restored After Groundbreaking Gene Therapy
An 18-month-old British girl who was born completely deaf is believed to be the youngest person to have their hearing restored after undergoing groundbreaking new gene therapy.
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Pfizer Pauses Gene Therapy Trial For Muscle Disease After Death
Pfizer Inc. paused a study of an experimental gene therapy for muscular dystrophy after a child who received it died suddenly.
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At $3.5 Million A Dose, This Is The World's Most Expensive Medicine
US regulators approved CSL Behring's hemophilia B gene therapy, a one-off infusion that frees patients from regular treatments but costs $3.5 million a dose, making it the most expensive medicine in the world.
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New Research Suggests Gene Therapy Could Be Used To Treat Pitt-Hopkins Syndrome
Postnatal gene therapy may be able to prevent or repair many of the harmful effects of Pitt-Hopkins syndrome, a rare genetic condition, according to researchers at the University of North Carolina School of Medicine. In an animal model of Pitt-Hopkins syndrome, researchers discovered that restoring lost gene activity eliminates numerous clinical in...
-
New Gene Therapy Uses Harmless Virus To Target Muscle Spasms, Study Finds
The findings showed that animals receiving the treatment experienced a gradual reduction in muscle spasticity. Significant improvements began to appear several weeks after therapy and continued over time.
-
Scientists Develop Targeted Drug Delivery For Arresting Tumour Growth, Reducing Off-target Effects
Experiments in breast cancer models demonstrated a robust gene knockdown, resulting in an increased cancer cell death and a substantial inhibition in tumour growth.
-
Biotech Firm MedTherapy Says It Can Cut Gene Therapy Production Time To One Day
A key claim by the company MedTherapy is a major reduction in production timelines. While gene therapies typically take weeks or months to manufacture, MedTherapy says it has significantly shortened the process.
-
New One-Shot Gene Editing Therapy May Reduce Bad Cholesterol By 62%
A groundbreaking gene-editing therapy developed by Eli Lilly and Verve Therapeutics reduced "bad" LDL cholesterol by up to 62% after a single infusion in an early trial, raising hopes for a long-lasting treatment to reduce heart attack risk
-
A New Gene Therapy May Restore Hearing In Weeks, Give People Born Deaf A Chance To Hear Again
The treatment targets a specific type of inherited deafness caused by mutations in a gene called OTOF.
-
India's BioE3 Policy Is Advancing GeneEditing And Cell Therapy: Minister
The first-in-human Phase-I clinical trial for gene therapy of Hemophilia A has shown clinically significant outcomes.
-
India Launches 1st Indigenous, Low-Cost Gene Therapy For Sickle Cell Disease
The world-class, low-cost gene editing solution named "BIRSA 101", in honour of Bhagwan Birsa Munda, remembered as a great tribal freedom fighter.
-
Scientists Restore Ancient Gene To Help Treat Gout And Uric Acid Disorders
Scientists at Georgia State University have revived a 20-million-year-old gene called uricase, which may offer new hope in treating gout and related uric acid disorders by helping the body break down excess uric acid naturally.
-
Indian-Made Gene Therapy For Blood Cancer Shows 73% Response Rate In Clinical Trials
An indigenously developed gene therapy for specific blood cancers has shown a 73 per cent response rate among patients in India, according to results of clinical trials published in The Lancet Haematology journal.
-
GST Council Exempts Gene Therapy, Cuts Tax Rate For Rice Kernels
Jaisalmer (Rajasthan): Union Finance Minister Nirmala Sitharaman on Saturday announced that the Goods and Services Tax Council has approved the reduction of GST on rice kernels to 5 per cent and exempted life-saving gene therapy from tax.
-
AI Unlocks “DNA Grammar” for Targeted Gene Editing, Enhancing Gene Therapy, and More
Researchers at The Jackson Laboratory, Broad Institute, and Yale University use AI to identify DNA sequences that control gene activation in specific cells. This AI model decodes patterns in DNA regions called cis-regulatory elements (CREs), guiding synthetic DNA switches for cell-specific gene activity. Early testing in animal models showed succes...
-
1-Year-Old UK Girl's Hearing Restored After Groundbreaking Gene Therapy
An 18-month-old British girl who was born completely deaf is believed to be the youngest person to have their hearing restored after undergoing groundbreaking new gene therapy.
-
Pfizer Pauses Gene Therapy Trial For Muscle Disease After Death
Pfizer Inc. paused a study of an experimental gene therapy for muscular dystrophy after a child who received it died suddenly.
-
At $3.5 Million A Dose, This Is The World's Most Expensive Medicine
US regulators approved CSL Behring's hemophilia B gene therapy, a one-off infusion that frees patients from regular treatments but costs $3.5 million a dose, making it the most expensive medicine in the world.
-
New Research Suggests Gene Therapy Could Be Used To Treat Pitt-Hopkins Syndrome
Postnatal gene therapy may be able to prevent or repair many of the harmful effects of Pitt-Hopkins syndrome, a rare genetic condition, according to researchers at the University of North Carolina School of Medicine. In an animal model of Pitt-Hopkins syndrome, researchers discovered that restoring lost gene activity eliminates numerous clinical in...
