Gene Therapy Drug
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Rare Epilepsy Breakthrough: Why This New Treatment Is Reducing Seizure Frequency In Children By 91%
An international clinical trial has achieved a new effective treatment option for rare epilepsy that can reduce seizures by 91% in children. Here is what this breakthrough means for the children suffering from Dravet Syndrome.
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Budget 2026: Middle Class Set To Gain From Affordable Healthcare, Says Dr Jitendra Singh
Affordable drugs, vaccines and diagnostics, supported by domestic biomanufacturing, would be a major social and economic support, especially for the middle class and vulnerable sections, said Union Minister of State.
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Top Scientific Discoveries Of 2025: A Year of Quantum Leaps And Cosmic Revelations
Here's a look at scientific discoveries and breakthroughs that made headlines in 2025, spanning space, biology, ecology, and fundamental physics.
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US Drug Regulator's Ousted Vaccine Chief Vinay Prasad Is Returning To Agency
A Food and Drug Administration official is getting his job back as the agency's top vaccine regulator, less than two weeks after he was pressured to step down at the urging of biotech executives, patient groups and conservative allies of Trump.
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Indian-Made Gene Therapy For Blood Cancer Shows 73% Response Rate In Clinical Trials
An indigenously developed gene therapy for specific blood cancers has shown a 73 per cent response rate among patients in India, according to results of clinical trials published in The Lancet Haematology journal.
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Gujarat Couple Raise Rs 16 Crore For 1 Injection To Save 5-Month-Old Son
A couple from Gujarat has raised Rs 16 crore with the help of a crowdfunding platform to buy a gene therapy injection for the treatment of their 5-month-old son suffering from spinal muscular atrophy, a rare genetic disorder.
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Just Approved Gene Therapy Drug Is World's Most Expensive At $2.1 Million
The Food and Drug Administration on Friday approved the most expensive drug in the world, a $2.1 million, one-time gene therapy for treatment of a rare disease that afflicts infants.
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Indian-US Team Identifies Genetic Target for Treating Colorectal Cancer
Making strides in the treatment of colorectal cancer (CRC), the third most common cancer in the world, a team of researchers from India and the US has identified a genetic target for potential drug therapy against the dreaded disease.
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Scientists reverse memory loss in mice with Alzheimer's
Spanish scientists have for the first time used gene therapy to reverse memory loss in mice with Alzheimer's, an advance that could lead to new drugs to treat the disease, they said on Wednesday.
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Sound waves to treat brain diseases
Sound waves could play a key role in helping to get drugs into the brain. Scientists have developed a method to open the blood-brain barrier temporarily to allow the entry of drugs and gene therapy to different specific brain areas.
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Rare Epilepsy Breakthrough: Why This New Treatment Is Reducing Seizure Frequency In Children By 91%
An international clinical trial has achieved a new effective treatment option for rare epilepsy that can reduce seizures by 91% in children. Here is what this breakthrough means for the children suffering from Dravet Syndrome.
-
Budget 2026: Middle Class Set To Gain From Affordable Healthcare, Says Dr Jitendra Singh
Affordable drugs, vaccines and diagnostics, supported by domestic biomanufacturing, would be a major social and economic support, especially for the middle class and vulnerable sections, said Union Minister of State.
-
Top Scientific Discoveries Of 2025: A Year of Quantum Leaps And Cosmic Revelations
Here's a look at scientific discoveries and breakthroughs that made headlines in 2025, spanning space, biology, ecology, and fundamental physics.
-
US Drug Regulator's Ousted Vaccine Chief Vinay Prasad Is Returning To Agency
A Food and Drug Administration official is getting his job back as the agency's top vaccine regulator, less than two weeks after he was pressured to step down at the urging of biotech executives, patient groups and conservative allies of Trump.
-
Indian-Made Gene Therapy For Blood Cancer Shows 73% Response Rate In Clinical Trials
An indigenously developed gene therapy for specific blood cancers has shown a 73 per cent response rate among patients in India, according to results of clinical trials published in The Lancet Haematology journal.
-
Gujarat Couple Raise Rs 16 Crore For 1 Injection To Save 5-Month-Old Son
A couple from Gujarat has raised Rs 16 crore with the help of a crowdfunding platform to buy a gene therapy injection for the treatment of their 5-month-old son suffering from spinal muscular atrophy, a rare genetic disorder.
-
Just Approved Gene Therapy Drug Is World's Most Expensive At $2.1 Million
The Food and Drug Administration on Friday approved the most expensive drug in the world, a $2.1 million, one-time gene therapy for treatment of a rare disease that afflicts infants.
-
Indian-US Team Identifies Genetic Target for Treating Colorectal Cancer
Making strides in the treatment of colorectal cancer (CRC), the third most common cancer in the world, a team of researchers from India and the US has identified a genetic target for potential drug therapy against the dreaded disease.
-
Scientists reverse memory loss in mice with Alzheimer's
Spanish scientists have for the first time used gene therapy to reverse memory loss in mice with Alzheimer's, an advance that could lead to new drugs to treat the disease, they said on Wednesday.
-
Sound waves to treat brain diseases
Sound waves could play a key role in helping to get drugs into the brain. Scientists have developed a method to open the blood-brain barrier temporarily to allow the entry of drugs and gene therapy to different specific brain areas.
