Gene Editing Therapy
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US Infant With Rare Disease First To Get Personalised Gene Therapy Treatment
A US infant with a rare condition has become history's first patient to be treated with a personalized gene-editing technique that raises hopes for other people with obscure illnesses, doctors said Thursday.
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AI Unlocks “DNA Grammar” for Targeted Gene Editing, Enhancing Gene Therapy, and More
Researchers at The Jackson Laboratory, Broad Institute, and Yale University use AI to identify DNA sequences that control gene activation in specific cells. This AI model decodes patterns in DNA regions called cis-regulatory elements (CREs), guiding synthetic DNA switches for cell-specific gene activity. Early testing in animal models showed succes...
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Innovative mRNA Delivery Technique Could Correct Genetic Disorders Before Birth
A recent study from UC Davis and UC Berkeley has unveiled a groundbreaking mRNA delivery method capable of editing genes in fetal brain cells. By administering mRNA encapsulated in lipid nanoparticles, researchers successfully targeted genetic disorders such as Angelman syndrome before birth. This approach, which minimizes risks of inflammation, of...
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Tech Millionaire Claims He ''Edited'' His DNA On Secret Island To ''Live Forever''
He explained that he believes the human lifespan is capped at 120 years, and gene therapy might hold the key to surpassing this limit.
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New Research Suggests Gene Therapy Could Be Used To Treat Pitt-Hopkins Syndrome
Postnatal gene therapy may be able to prevent or repair many of the harmful effects of Pitt-Hopkins syndrome, a rare genetic condition, according to researchers at the University of North Carolina School of Medicine. In an animal model of Pitt-Hopkins syndrome, researchers discovered that restoring lost gene activity eliminates numerous clinical in...
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Tata Memorial Hospital, IIT Bombay Collaborate for ‘First in India’ CAR-T Cell Therapy for Cancer Treatment
Tata Memorial Hospital and IIT Bombay collaborated for the first Chimeric Antigen Receptor T-cell (CAR-T) therapy, a type of gene therapy for blood cancer treatment, in India, which was conducted on Friday, June 4 in Mumbai.
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2020 Nobel Prize in Chemistry Awarded for CRISPR/Cas9 'Genetic Scissors'
Two women scientists - Emmanuelle Charpentier, who is French, and American Jennifer Doudna - won the 2020 Nobel Prize in Chemistry on Wednesday for creating genetic 'scissors' that can rewrite the code of life, contributing to new cancer therapies and holding out the prospect of curing hereditary diseases.
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Alphabet's GV Leads Funding in Gene Editing Company Verve Therapeutics
GV led a $58.5 million investment to launch Verve Therapeutics, a new biotech focused on developing therapies that edit the human genome to treat heart diseases.
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CRISPR Gene Editing Can Cause Risky Collateral DNA Damage: Study
The findings have safety implications for gene therapies that are being developed using CRISPR/Cas9.
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US Infant With Rare Disease First To Get Personalised Gene Therapy Treatment
A US infant with a rare condition has become history's first patient to be treated with a personalized gene-editing technique that raises hopes for other people with obscure illnesses, doctors said Thursday.
-
AI Unlocks “DNA Grammar” for Targeted Gene Editing, Enhancing Gene Therapy, and More
Researchers at The Jackson Laboratory, Broad Institute, and Yale University use AI to identify DNA sequences that control gene activation in specific cells. This AI model decodes patterns in DNA regions called cis-regulatory elements (CREs), guiding synthetic DNA switches for cell-specific gene activity. Early testing in animal models showed succes...
-
Innovative mRNA Delivery Technique Could Correct Genetic Disorders Before Birth
A recent study from UC Davis and UC Berkeley has unveiled a groundbreaking mRNA delivery method capable of editing genes in fetal brain cells. By administering mRNA encapsulated in lipid nanoparticles, researchers successfully targeted genetic disorders such as Angelman syndrome before birth. This approach, which minimizes risks of inflammation, of...
-
Tech Millionaire Claims He ''Edited'' His DNA On Secret Island To ''Live Forever''
He explained that he believes the human lifespan is capped at 120 years, and gene therapy might hold the key to surpassing this limit.
-
New Research Suggests Gene Therapy Could Be Used To Treat Pitt-Hopkins Syndrome
Postnatal gene therapy may be able to prevent or repair many of the harmful effects of Pitt-Hopkins syndrome, a rare genetic condition, according to researchers at the University of North Carolina School of Medicine. In an animal model of Pitt-Hopkins syndrome, researchers discovered that restoring lost gene activity eliminates numerous clinical in...
-
Tata Memorial Hospital, IIT Bombay Collaborate for ‘First in India’ CAR-T Cell Therapy for Cancer Treatment
Tata Memorial Hospital and IIT Bombay collaborated for the first Chimeric Antigen Receptor T-cell (CAR-T) therapy, a type of gene therapy for blood cancer treatment, in India, which was conducted on Friday, June 4 in Mumbai.
-
2020 Nobel Prize in Chemistry Awarded for CRISPR/Cas9 'Genetic Scissors'
Two women scientists - Emmanuelle Charpentier, who is French, and American Jennifer Doudna - won the 2020 Nobel Prize in Chemistry on Wednesday for creating genetic 'scissors' that can rewrite the code of life, contributing to new cancer therapies and holding out the prospect of curing hereditary diseases.
-
Alphabet's GV Leads Funding in Gene Editing Company Verve Therapeutics
GV led a $58.5 million investment to launch Verve Therapeutics, a new biotech focused on developing therapies that edit the human genome to treat heart diseases.
-
CRISPR Gene Editing Can Cause Risky Collateral DNA Damage: Study
The findings have safety implications for gene therapies that are being developed using CRISPR/Cas9.
